Icandelo lokuphuhlisa nokuthengisa imishishini yinkampani enkulu, kunye neenkampani ezizisa iibhiliyoni kwingeniso yonyaka. Ehlabathini lonke, ukuthengiswa kwezidakamizwa zonyango kulindeleke ukuba kudlule i-$ 1.3 trillion ngo-2018. Ukuthengiswa kwe-Pharma kukhulu kunomkhiqizo wekhaya owenziwe ngamazwe angama-15, idibeneyo. Kwabanye abantu, ngakumbi abo banezifo ezingaqhelekanga, iindleko zala mayeza enyantya zinokuthandwa. Iziyobisi zengcwaba, imichiza eyenzelwe ukunyanga izifo ezithathwa ngabantu abambalwa kuphela, zinokubhatala ngokulula kumanani amathandathu.
Ezinye iinkampani ze-inshorensi aziyi kugubungela yonke into okanye inxalenye ebalulekileyo yalezi yobisi, ukushiya intsapho kunye nabantu abachaphazelekayo ukuba baphathe iindleko ngokwabo. Lo ngumthwalo obalulekileyo wemali kwabaninzi kwaye ubangele ukuhlolisisa kakhulu kwi-shishini.
Amanye amanyathelo asetyenziswe ukukhupha iindleko, njengemibutho engekho inzuzo kunye neenkqubo zoncedo zoncedo. Nangona ezi zinokuba luncedo kwabanye, ipesenteji enkulu yabantu ayifanelekanga kwaye kufuneka ihlawule ipokothini kule miyeza yokulondoloza ubomi.
01 Glybera
Umenzi walo, UniQure, wathi ngo-2017 ukuba kwakungayi kuba kuhlaziywa kwegunya lokuthengisa izidakamizwa eYurophu. Nangona ixabiso lentengo ephezulu, uGlybera akazange abanjwe ngenxa yokufunwa komonde.
02 Soliris
I-Soliris inokugulisa izigulane ukuya kwii-700,000 zamawaka ngonyaka, isisetyenziswa esisetyenziswayo ukunyanga i-hemoglobinuria ye-paroxysmal nocturnal. Abantu abayi-8 000 kuphela kwihlabathi banemeko. Isi sifo sitshabalalisa iiseli ezibomvu zegazi, ezibangela izigulane ukuba zibe ne-infections, i-anemia, kunye nama-blood clots.
NgoSeptemba 2017, amagunya aseCanada ayala umenzi we-Alexion Pharmaceuticals ukuba anciphise intengo ka-Soliris, ebiza ngokuba yinto engaphezulu.
03 Ukuhlaselwa
I-Elaprase isetyenziselwa ukuphatha i-Hunter Syndrome, imeko engaqhelekiyo echaphazelekayo kubantu abangama-500 e-United States ekhusela umsebenzi wengqondo kunye nophuhliso lomzimba. Iindleko zonyaka zonyango zingaphezu kwama-500,000.
04 Naglazyme
I-Naglazyme isetyenziselwa ukunyanga iMaroteaux-Lamy Syndrome, imeko echaphazela izicubu ezinxulumene. Iimpawu eziqhelekileyo ziquka ukutshatyalaliswa kwezinto, ukukhutshwa, ukukhutshwa, ukukhathazeka, ukukhathazeka kweengxaki kunye nentlungu engqondweni. Iyeza libiza ngaphezu kwama-365,000.
05 Cinryze
I-Cinryze isebenzela imeko ebizwa nge-angioedema, isifo esichaphazela omnye kubantu abangama-50,000 e-United States. Kwindleko ye-$ 350,000 ngonyaka, iyeza lilawula ukuvuvukala kwezandla, umhombo, nesisu.
06 Folotyn
I-Folotyn yonyango lwenqweno engavumelekanga yomhlaza obizwa ngeT-cell lymphoma. Kuthathwa njengenyango yokugqibela yonyango ehlala kwiiveki ezintandathu. Ngeendleko ezingaphezu kwama-320,000, ayizange iboniswe ukunyusa ubomi ixesha elide, ngoko isetyenziswa rhoqo kwiimeko ezimbi kuphela.
07 Acthar
U-Acthar unqunywe ukuba uphathwe ngokukhawuleza okanye ukuxhamla. Le meko ichaphazela abantwana phakathi kweminyaka emine ne-11 ubudala, kodwa u-Acthar uvunyiwe ukuphatha abantwana ukuya kwiminyaka emibini ubudala. Kwakhona kusetyenziswa ukunyanga iindidi ezahlukeneyo kubantu abadala, kubandakanywa i-multiple sclerosis. Ixabisa ngaphezu kwama-200,000 ngonyaka.
Ucwaningo lwango-2017 kwi-Journal ye-American Medical Associaton lubuze ukuphumelela kuka-Acthar, ebonisa ukuba ayiphumelelanga ngakumbi kunezinye iindleko eziphantsi kakhulu.
08 Myozyme
I-Myozyme yonyango lwePompe, isifo esingaqhathananga nesinye isifo esihlasela intliziyo kunye nezihlunu zesifo. Xa ichaphazela iintsana, ukufa kufuthi kubetha ngonyaka wokuqala. I-Myozyme yi-enzyme ethile ye-lysosomal glycogen ebonisa ukuba kwizifundo zandise ukuphila kwaye zanciphisa izigulane zithembele kwiindawo zokuqhuba umoya. Iindleko zayo zonyaka ziphakathi kwe-100,000 ne-300,000 zamawaka ngonyaka. Okwamanje ayitholakali e-US